{"id":3350,"date":"2025-05-19T12:32:17","date_gmt":"2025-05-19T12:32:17","guid":{"rendered":"https:\/\/life4hsp.com\/?p=3350"},"modified":"2025-09-29T19:47:16","modified_gmt":"2025-09-29T17:47:16","slug":"ricerca-trattamento-per-la-spg11-avviata","status":"publish","type":"post","link":"https:\/\/life4hsp.com\/it\/ricerca-trattamento-per-la-spg11-avviata\/","title":{"rendered":"La ricerca per un trattamento della SPG11 \u00e8 iniziata con il supporto di Life4HSP ed Euro-HSP."},"content":{"rendered":"<p>A partire da marzo 2025, Euro-HSP, insieme a Life4HSP, ha avviato il supporto a un nuovo progetto di ricerca per SPG11. Questo progetto \u00e8 volto a trovare un trattamento per SPG11, una forma rara ed ereditaria di HSP (Paraparesi spastica ereditaria). Anche forme correlate come SPG15 e SPG48 rientrano in questa ricerca. Con ci\u00f2, ampliamo il nostro impegno oltre al progetto euroSPG4 gi\u00e0 in corso.<\/p>\n<h3>Il farmaco Venglustat, un possibile trattamento promettente<\/h3>\n<p>La ricerca si svolge presso il Paris Brain Institute in Francia, sotto la guida del dottor Fr\u00e9d\u00e9ric Darios. I ricercatori stanno testando un medicinale gi\u00e0 esistente, il Venglustat, che potrebbe aiutare a rallentare la progressione della malattia nell\u2019SPG11. I primi risultati in laboratorio sono incoraggianti. In uno studio preclinico si valuta se il farmaco \u00e8 sicuro ed efficace a lungo termine. L\u2019intero processo dura due anni.<\/p>\n<p>\u00c8 stato scoperto che, nei casi di SPG11, SPG15 e SPG48, si verifica un problema nelle cellule nervose: non riescono a degradare correttamente alcune sostanze \u2013 i gangliosidi. Queste sostanze si accumulano nelle cellule e causano danni al sistema nervoso. Il Venglustat sembra aiutare riducendo la produzione di queste sostanze dannose.<\/p>\n<h3>Grazie ai donatori, il progetto ha gi\u00e0 potuto iniziare.<\/h3>\n<p>Per realizzare questa ricerca, \u00e8 necessario un importo di quasi 200.000 \u20ac distribuito su due anni. Grazie ai nostri donatori e a un importante contributo da parte di Life4HSP, Euro-HSP ha potuto avviare il progetto con un primo pagamento di 60.000 \u20ac. Ne siamo profondamente grati.<\/p>\n<p>Inoltre, sono necessari fondi anche per un\u2019altra ricerca importante: lo sviluppo di un biomarcatore. Si tratta di una sorta di \u201cstrumento di misurazione\u201d che consente ai medici di verificare se un trattamento ha effetto. Senza un biomarcatore, \u00e8 difficile stabilire se un farmaco funziona davvero. Life4HSP e la nostra organizzazione partner stopp-HSP dall\u2019Austria sostengono congiuntamente una ricerca sui biomarcatori presso il rinomato Children\u2019s Hospital di Harvard (USA). Questo progetto riceve un contributo di 10.000 \u20ac.<\/p>\n<p>Oltre a queste nuove attivit\u00e0, anche il progetto euroSPG4 continua a svilupparsi. A nome di Life4HSP, desideriamo ringraziare tutti i nostri donatori.<\/p>\n<p><strong>Vuoi contribuire a ulteriori ricerche?<\/strong><\/p>\n<p>Allora visita la nostra piattaforma per le donazioni: <a href=\"https:\/\/life4hsp.community-fundraising.com\/donate?locale=it\" target=\"_blank\" rel=\"noopener\">https:\/\/life4hsp.community-fundraising.com\/donate?locale=it<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p>Vanaf maart 2025 is Euro-HSP, samen met Life4HSP, gestart met de ondersteuning van een nieuw onderzoeksproject voor SPG11. Dit project richt zich op het vinden van een behandeling voor SPG11, een zeldzame en erfelijke vorm van HSP (Hereditaire spastische paraparese). Ook verwante vormen zoals SPG15 en SPG48 vallen binnen dit onderzoek. Hiermee breiden we onze [&hellip;]<\/p>\n","protected":false},"author":2,"featured_media":3351,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"_acf_changed":false,"inline_featured_image":false,"footnotes":""},"categories":[13],"tags":[],"class_list":["post-3350","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-onderzoek"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.9 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>SPG11-onderzoek<\/title>\n<meta name=\"description\" content=\"Met steun van Life4HSP is onderzoek gestart naar een behandeling voor SPG11. Venglustat toont hoopvolle resultaten. 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